Duchenne muscular dystrophy with Kocher-Debre-Semelaigne syndrome: a double jeopardy., PMID:40466673
Polymer-based coating of adeno-associated viral particles as a new strategy to evade immune response for DMD treatment., PMID:40441494
Pilot study of canakinumab (Ilaris) in steroid naïve children with Duchenne muscular dystrophy demonstrates safety and exploratory changes in potential serum protein response biomarkers., PMID:40396427
Clinical applications of exon-skipping antisense oligonucleotides in neuromuscular diseases., PMID:40308063
Anti-fibrotic, muscle-promoting antibody-drug conjugates for the improvement and treatment of DMD., PMID:40276765
AOC 1044 induces exon 44 skipping and restores dystrophin protein in preclinical models of Duchenne muscular dystrophy., PMID:40183632
Case Report: Ofatumumab treatment for concomitant multiple sclerosis and idiopathic thrombocytopenic purpura., PMID:40134425
Long-term preservation of muscle function and structure by repeated administration of cardiosphere-derived cells in mdx mice., PMID:40118057
Enhancing AAV-microdystrophin gene therapy after repeat dosing by blocking phagocytosis., PMID:40098958
The effect of IL-1β inhibitor canakinumab (Ilaris®) on IL-6 production in human skeletal muscle cells., PMID:40048444
Targeting Drug Delivery System to Skeletal Muscles: A Comprehensive Review of Different Approaches., PMID:39910928
Inhibition of hippocampal interleukin-6 receptor-evoked signalling normalises long-term potentiation in dystrophin-deficient mdx mice., PMID:39867844
Cytotoxic T-Lymphocyte-Associated Protein 4 Fused to a Modified Fragment of IgG1 Reduces Muscle Fiber Damage in a Model of Duchenne Muscular Dystrophy by Attenuating Proinflammatory Gene Expression in Myeloid Lineage Cells., PMID:39814100
Relationship Between Quantitative Magnetic Resonance Imaging Measures and Functional Changes in Patients With Duchenne Muscular Dystrophy., PMID:39713935
Prevalence of Neutralizing Antibodies Against AAV Serotypes 2 and 9 in Healthy Participants from Multiple Centers Across China and Patients with DMD/BMD., PMID:39607725
Redundancy in Innate Immune Pathways That Promote CD8+ T-Cell Responses in AAV1 Muscle Gene Transfer., PMID:39459842
[Deflazacort-induced Steven-Johnson syndrome: a case report and literature review]., PMID:39429084
CTLA4 blockade abrogates KEAP1/STK11-related resistance to PD-(L)1 inhibitors., PMID:39385035
A potent pan-sarbecovirus neutralizing antibody resilient to epitope diversification., PMID:39383863
Efficient α and β- radionuclide therapy targeting fibroblast activation protein-α in an aggressive preclinical mouse tumour model., PMID:39237746
Structure-Activity Relationship of Antibody-Oligonucleotide Conjugates: Evaluating Bioconjugation Strategies for Antibody-Phosphorodiamidate Morpholino Oligomer Conjugates for Drug Development., PMID:39197837
What is in the Myopathy Literature?, PMID:39163158
Adrenal Suppression From Vamorolone and Prednisone in Duchenne Muscular Dystrophy: Results From the Phase 2b Clinical Trial., PMID:39097643
Generic semi-automated radiofluorination strategy for single domain antibodies: [18F]FB-labelled single domain antibodies for PET imaging of fibroblast activation protein-α or folate receptor-α overexpression in cancer., PMID:39048805
Circulating KRAS G12D but not G12V is associated with survival in metastatic pancreatic ductal adenocarcinoma., PMID:38982051
A universal urinary cell gene signature of acute rejection in kidney allografts., PMID:38936464
Cytokine Levels in Experimental Branch Retinal Vein Occlusion Treated With Either Bevacizumab or Triamcinolone Acetonide., PMID:38899953
Practical Considerations for Delandistrogene Moxeparvovec Gene Therapy in Patients With Duchenne Muscular Dystrophy., PMID:38306745
TMEM106B core deposition associates with TDP-43 pathology and is increased in risk SNP carriers for frontotemporal dementia., PMID:38232138
Adverse Events Associated With Disease-Modifying Drugs for Multiple Sclerosis: A Multiregional Population-Based Study., PMID:38181306
Precision medicine using whole genome sequencing identifies a novel dystrophin (DMD) variant for X-linked muscular dystrophy in a cat., PMID:38180235
Prevalence of Adeno-Associated Virus-9-Neutralizing Antibody in Chinese Patients with Duchenne Muscular Dystrophy., PMID:38084965
[Multiple sclerosis and melanoma]., PMID:37966451
Multiplex Bioanalytical Methods for Comprehensive Characterization and Quantification of the Unique Complementarity-Determining-Region Deamidation of MEDI7247, an Anti-ASCT2 Pyrrolobenzodiazepine Antibody-Drug Conjugate., PMID:37873863
Immunoglobulin levels are higher at multiple sclerosis onset - a part of natural history?, PMID:37806232
Safety and durable immunogenicity of the TV005 tetravalent dengue vaccine, across serotypes and age groups, in dengue-endemic Bangladesh: a randomised, controlled trial., PMID:37776876
Corticosteroid-induced low immunoglobulin levels in multiple sclerosis - A confounding factor., PMID:37774601
Oral and IV Varespladib Rescue Experiments in Juvenile Pigs with Weakness Induced by Australian and Papuan Oxyuranus scutellatus Venoms., PMID:37755983
Death after High-Dose rAAV9 Gene Therapy in a Patient with Duchenne's Muscular Dystrophy., PMID:37754285
Safety and Efficacy of DT-DEC01 Therapy in Duchenne Muscular Dystrophy Patients: A 12 - Month Follow-Up Study After Systemic Intraosseous Administration., PMID:37707670
A highly sensitive and quantitative assay for dystrophin protein using Single Molecule Count Technology., PMID:37666691
Tetraspanin CD82 Associates with Trafficking Vesicle in Muscle Cells and Binds to Dysferlin and Myoferlin., PMID:37434585
Viewpoint: Clinicians' Perspectives on How Disease Modifying Drugs for Alzheimer's Disease Impact Specialty Care., PMID:37357267
Orthogonal proteomics methods warrant the development of Duchenne muscular dystrophy biomarkers., PMID:37308827
Design single-stranded DNA aptamer of cluster of differentiation 47 protein by stochastic tunnelling-basin hopping-discrete molecular dynamics method., PMID:37261868
Pamrevlumab, a Fully Human Monoclonal Antibody Targeting Connective Tissue Growth Factor, for Non-Ambulatory Patients with Duchenne Muscular Dystrophy., PMID:37248912
Optimizing the Production of gp145, an HIV-1 Envelope Glycoprotein Vaccine Candidate and Its Encapsulation in Guanosine Microparticles., PMID:37243079
Innovative Computerized Dystrophin Quantification Method Based on Spectral Confocal Microscopy., PMID:37047330
A Proof of Principle Proteomic Study Detects Dystrophin in Human Plasma: Implications in DMD Diagnosis and Clinical Monitoring., PMID:36982290
A low dose of RBD and TLR7/8 agonist displayed on influenza virosome particles protects rhesus macaque against SARS-CoV-2 challenge., PMID:36977691
For research use only. Not for human or drug use.
